Cell-Seq – a unique tool to find new drug targets for unmet medical needs
Modifier genes — compensatory genes that counteract the effect of a disease-causing gene
Modifier genes explain why some people with genetic mutations linked to severe disease have only mild or no symptoms. Modifier genes therefore positively influence the severity of disease and act as a ‘natural form of protection’. To date, modifier genes or compensatory genes have been difficult to identify, especially for genetic disorders. Now, for the first time, Scenic is systemically exploring modifier genes using its proprietary platform technology for a large variety of disorders, including inherited diseases.
Our Cell-Seq™ platform enables high-resolution mapping of modifier genes for novel target discovery
Scenic Biotech has overcome the technical challenges of reliably finding modifier genes or the “hidden disease protection factors” using Cell-Seq, its unique discovery platform. Using functional genomics, Cell-Seq can create high-resolution disease maps that profile previously uncharted biological pathways and disease biology in an unprecedented fashion. This allows to uncover completely novel, potent drug targets that form the basis for Scenic’s rapidly growing pipeline of novel disease therapeutics. We also leverage the power of Cell-Seq and its associated data warehouse in collaborations with pharma partners.
With Cell-Seq, we are enabling the development of disease-modifying therapeutics for devastating genetic diseases.
We are building the largest proprietary data warehouse of modifier genes.
We have identified novel modifier genes for over a dozen diseases and built a robust pipeline of first-in-class small molecule inhibitors based on these new drug targets. Discover our ongoing programs of discovery, development and collaborations!